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590
datasets available to search
ShareScore release 0.9.0
Dataset results
590 results for “muscular dystrophies.”
Use of (-)-Epicatechin in the Treatment of Becker Muscular Dystrophy (Pilot Study)
ClinicalTrials.gov study NCT01856868. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Study of ACE-083 in Patients With Facioscapulohumeral Muscular Dystrophy (FSHD)
ClinicalTrials.gov study NCT02927080. IPD Sharing: Not stated. Countries: 3. Publications: 0.
Safety Study of Eteplirsen to Treat Advanced Stage Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT02286947. IPD Sharing: Not stated. Countries: 1. Publications: 0.
A Study to Assess the Efficacy and Safety of MNK-1411 in Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03400852. IPD Sharing: NO. Countries: 8. Publications: 0.
A Study of TAS-205 for Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT02246478. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Safety and Efficacy Study of IGF-1 in Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT01207908. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Study to Evaluate the Long-Term Safety, Tolerability, and Biological Activity of ATYR1940 in Participants With Limb Girdle and Facioscapulohumeral Muscular Dystrophy (FSHD)
ClinicalTrials.gov study NCT02836418. IPD Sharing: NO. Countries: 3. Publications: 0.
Proof of Concept Study to Assess Activity and Safety of SMT C1100 (Ezutromid) in Boys With Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT02858362. IPD Sharing: Not stated. Countries: 2. Publications: 0.
Myocardial Fibrosis Progression in Duchenne and Becker Muscular Dystrophy - ACE Inhibitor Therapy Trial
ClinicalTrials.gov study NCT02432885. IPD Sharing: Not stated. Countries: 0. Publications: 1.
A Study of Deflazacort (Emflaza®) in Participants With Limb-Girdle Muscular Dystrophy 2I (LGMD2I)
ClinicalTrials.gov study NCT03783923. IPD Sharing: Not stated. Countries: 8. Publications: 0.
Study of Ataluren (PTC124) in Nonambulatory Participants With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD)
ClinicalTrials.gov study NCT01009294. IPD Sharing: NO. Countries: 2. Publications: 0.
A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)
ClinicalTrials.gov study NCT03648827. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Study of ACE-031 in Subjects With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT01099761. IPD Sharing: NO. Countries: 1. Publications: 0.
Extension Study of NS-065/NCNP-01 in Boys With Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT03167255. IPD Sharing: NO. Countries: 2. Publications: 0.
Improved Muscle Function in Duchenne Muscular Dystrophy Through L-Arginine and Metformin
ClinicalTrials.gov study NCT02516085. IPD Sharing: Not stated. Countries: 0. Publications: 1.
A Phase I/II, Open Label, Escalating Dose, Pilot Study to Assess Effect, Safety, Tolerability and PK of Multiple SC Doses of Drisapersen in Patients With Duchenne Muscular Dystrophy and to Assess the
ClinicalTrials.gov study NCT01910649. IPD Sharing: Not stated. Countries: 0. Publications: 2.
Expanded Access Protocol for Boys With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03863119. IPD Sharing: Not stated. Countries: 3. Publications: 0.
Sedation During Muscle Biopsy in Patients With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT01645098. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Bone Health in Facioscapulohumeral Muscular Dystrophy
ClinicalTrials.gov study NCT02413190. IPD Sharing: NO. Countries: 2. Publications: 0.
A Clinical Study to Assess Two Doses of GSK2402968 in Subjects With Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT01462292. IPD Sharing: Not stated. Countries: 1. Publications: 0.
ScienceDex guides
Understand access before you commit
These curated guides explain access requirements, typical timelines, costs, and reuse considerations for widely used research datasets.
Allen Brain Atlas
Allen Brain Atlas is an Allen Institute collection of brain map atlases, datasets, APIs, and analysis tools covering mouse, human, and non-human primate brain resources.
Annotated Behaviour and Observability Dataset (ABODe)
ABODe is a University of Edinburgh DataShare dataset for behavior classification in group-housed mice using home-cage video, identities, bounding boxes, ground-plate positions, and annotator labels.
DANDI Archive for NWB datasets
DANDI is a BRAIN Initiative archive for publishing and sharing neurophysiology data, including electrophysiology, optophysiology, and behavioral data packaged as NWB and related standards.
International Brain Laboratory public data
The International Brain Laboratory public data releases expose standardized mouse decision-making experiments, including Neuropixels recordings, widefield calcium imaging, behavior, and session metadata accessed through the ONE API.
OpenNeuro
OpenNeuro is a free, open platform for sharing neuroimaging datasets, with public search, dataset pages, and download paths for web, S3, DataLad, and the OpenNeuro CLI.