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590
datasets available to search
ShareScore release 0.9.0
Dataset results
590 results for “muscular dystrophies.”
Evaluation of the Safety, Tolerability, and Efficacy of LE051 in Patients With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT06900049. IPD Sharing: NO. Countries: 1. Publications: 0.
Whole Body Vibration Therapy in Boys With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT01954940. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Nebivolol for the Prevention of Left Ventricular Systolic Dysfunction in Patients With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT01648634. IPD Sharing: Not stated. Countries: 1. Publications: 0.
LARA: Use of JACO2 Controlled by Joystick or by Voice Control System, in Muscular Dystrophy
ClinicalTrials.gov study NCT04313049. IPD Sharing: NO. Countries: 1. Publications: 0.
Extension Study of ACE-031 in Subjects With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT01239758. IPD Sharing: Not stated. Countries: 1. Publications: 0.
A Gene Transfer Study to Evaluate the Safety, Tolerability and Efficacy of SRP-6004 in Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2B/R2 (LGMD2B/R2, Dysferlin [DYSF] Related)
ClinicalTrials.gov study NCT05906251. IPD Sharing: Not stated. Countries: 1. Publications: 0.
A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4
ClinicalTrials.gov study NCT06246513. IPD Sharing: Not stated. Countries: 6. Publications: 0.
Limb Girdle Muscular Dystrophy (LGMD) Natural History
ClinicalTrials.gov study NCT01783509. IPD Sharing: Not stated. Countries: 1. Publications: 0.
A Study to Evaluate the Safety and Tolerability of RAG-18 in Pediatric Patients With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT07282652. IPD Sharing: NO. Countries: 1. Publications: 0.
Study to Evaluate the Efficacy and Safety of BBP-418 (Ribitol) in Patients With Limb Girdle Muscular Dystrophy 2I (LGMD2I)
ClinicalTrials.gov study NCT05775848. IPD Sharing: YES. Countries: 8. Publications: 0.
Pentoxifylline in Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT00102453. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Clinical Trial of Coenzyme Q10 and Lisinopril in Muscular Dystrophies
ClinicalTrials.gov study NCT01126697. IPD Sharing: Not stated. Countries: 3. Publications: 0.
Multiparametric Ultrafast Ultrasound Biomarkers for Duchenne and Becker Muscular Dystrophies
ClinicalTrials.gov study NCT07378553. IPD Sharing: Not stated. Countries: 0. Publications: 0.
A First-in-human Study of EPI-321 in Facioscapulohumeral Muscular Dystrophy
ClinicalTrials.gov study NCT06907875. IPD Sharing: NO. Countries: 3. Publications: 0.
An Open-Label Extension Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03917719. IPD Sharing: Not stated. Countries: 6. Publications: 0.
Observation Study in Patients Age 0-5 Years With LAMA2-related Congenital Muscular Dystrophy
ClinicalTrials.gov study NCT06503367. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Regular Physical Exercise in Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03963453. IPD Sharing: NO. Countries: 1. Publications: 0.
The Effect of Kinesiology Taping on Balance in Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03541070. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Gamified Occupational Therapy for Adolescents With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT06402942. IPD Sharing: NO. Countries: 1. Publications: 0.
Evaluation of Limb-Girdle Muscular Dystrophy
ClinicalTrials.gov study NCT00893334. IPD Sharing: Not stated. Countries: 1. Publications: 0.
ScienceDex guides
Understand access before you commit
These curated guides explain access requirements, typical timelines, costs, and reuse considerations for widely used research datasets.
Allen Brain Atlas
Allen Brain Atlas is an Allen Institute collection of brain map atlases, datasets, APIs, and analysis tools covering mouse, human, and non-human primate brain resources.
Annotated Behaviour and Observability Dataset (ABODe)
ABODe is a University of Edinburgh DataShare dataset for behavior classification in group-housed mice using home-cage video, identities, bounding boxes, ground-plate positions, and annotator labels.
DANDI Archive for NWB datasets
DANDI is a BRAIN Initiative archive for publishing and sharing neurophysiology data, including electrophysiology, optophysiology, and behavioral data packaged as NWB and related standards.
International Brain Laboratory public data
The International Brain Laboratory public data releases expose standardized mouse decision-making experiments, including Neuropixels recordings, widefield calcium imaging, behavior, and session metadata accessed through the ONE API.
OpenNeuro
OpenNeuro is a free, open platform for sharing neuroimaging datasets, with public search, dataset pages, and download paths for web, S3, DataLad, and the OpenNeuro CLI.