Find research datasets worth reusing
Search datasets from major research repositories and use ShareScore to quickly assess how well each record supports discovery, access, and reuse.
87
datasets available to search
ShareScore release 0.9.0
Dataset results
87 results for “mucopolysaccharidosis”
Underlying data for Prevalence Rates of Mucopolysaccharidosis in Iraq: a retrospective cross-sectional observational study
<p>Underlying data for Prevalence Rates of Mucopolysaccharidosis in Iraq: a retrospective cross-sectional observational study</p>
Natural History Study of Patients With Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B)
ClinicalTrials.gov study NCT01509768. IPD Sharing: Not stated. Countries: 3. Publications: 1.
Study to Detect Unrecognized Mucopolysaccharidosis in Children Visiting Rheumatology, Hand or Skeletal Dysplasia Clinics
ClinicalTrials.gov study NCT01675674. IPD Sharing: Not stated. Countries: 1. Publications: 30.
Gene Therapy with Modified Autologous Hematopoietic Stem Cells for Patients with Mucopolysaccharidosis Type IIIA
ClinicalTrials.gov study NCT04201405. IPD Sharing: NO. Countries: 1. Publications: 5.
A Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)
ClinicalTrials.gov study NCT00787995. IPD Sharing: Not stated. Countries: 10. Publications: 1.
Discovering New Biomarkers For Monitoring Disease Progression in Patients With Mucopolysaccharidosis IVA
ClinicalTrials.gov study NCT01733615. IPD Sharing: Not stated. Countries: 1. Publications: 2.
Parental Coping With Challenging Behavior in Mucopolysaccharidosis Type I-III
ClinicalTrials.gov study NCT03161171. IPD Sharing: NO. Countries: 1. Publications: 1.
Mucopolysaccharidosis I (MPS I) Registry
ClinicalTrials.gov study NCT00144794. IPD Sharing: Not stated. Countries: 40. Publications: 3.
Observational Study of Patients With Mucopolysaccharidosis (MPS) VI Who Previously Participated in ASB-00-02
ClinicalTrials.gov study NCT01387854. IPD Sharing: Not stated. Countries: 7. Publications: 1.
A Prospective Natural History Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)
ClinicalTrials.gov study NCT03227042. IPD Sharing: UNDECIDED. Countries: 9. Publications: 1.
Study of AAVrh10-h.SGSH Gene Therapy in Patients With Mucopolysaccharidosis Type IIIA (MPS IIIA)
ClinicalTrials.gov study NCT03612869. IPD Sharing: UNDECIDED. Countries: 5. Publications: 1.
A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)
ClinicalTrials.gov study NCT02493998. IPD Sharing: Not stated. Countries: 8. Publications: 1.
Gene Transfer Clinical Trial for Mucopolysaccharidosis (MPS) IIIB
ClinicalTrials.gov study NCT03315182. IPD Sharing: NO. Countries: 4. Publications: 17.
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
ClinicalTrials.gov study NCT00214773. IPD Sharing: NO. Countries: 13. Publications: 1.
A Study of JR-141 in Patients With Mucopolysaccharidosis Type II
ClinicalTrials.gov study NCT03128593. IPD Sharing: Not stated. Countries: 1. Publications: 1.
Gene Therapy With Modified Autologous Hematopoietic Stem Cells for the Treatment of Patients With Mucopolysaccharidosis Type I, Hurler Variant
ClinicalTrials.gov study NCT03488394. IPD Sharing: UNDECIDED. Countries: 1. Publications: 13.
Respiratory Cathepsins, Proteases Inhibitors and Glycosaminoglycans (GAG) in Mucopolysaccharidosis
ClinicalTrials.gov study NCT04112602. IPD Sharing: Not stated. Countries: 1. Publications: 9.
A Treatment Study of Mucopolysaccharidosis Type IIIB
ClinicalTrials.gov study NCT02754076. IPD Sharing: NO. Countries: 7. Publications: 2.
The Effect of Enzyme Replacement Therapy in Mucopolysaccharidosis
ClinicalTrials.gov study NCT05006222. IPD Sharing: NO. Countries: 1. Publications: 5.
Gene Therapy in Patients With Mucopolysaccharidosis Disease
ClinicalTrials.gov study NCT03173521. IPD Sharing: Not stated. Countries: 2. Publications: 2.
ScienceDex guides
Understand access before you commit
These curated guides explain access requirements, typical timelines, costs, and reuse considerations for widely used research datasets.
Allen Brain Atlas
Allen Brain Atlas is an Allen Institute collection of brain map atlases, datasets, APIs, and analysis tools covering mouse, human, and non-human primate brain resources.
Annotated Behaviour and Observability Dataset (ABODe)
ABODe is a University of Edinburgh DataShare dataset for behavior classification in group-housed mice using home-cage video, identities, bounding boxes, ground-plate positions, and annotator labels.
DANDI Archive for NWB datasets
DANDI is a BRAIN Initiative archive for publishing and sharing neurophysiology data, including electrophysiology, optophysiology, and behavioral data packaged as NWB and related standards.
International Brain Laboratory public data
The International Brain Laboratory public data releases expose standardized mouse decision-making experiments, including Neuropixels recordings, widefield calcium imaging, behavior, and session metadata accessed through the ONE API.
OpenNeuro
OpenNeuro is a free, open platform for sharing neuroimaging datasets, with public search, dataset pages, and download paths for web, S3, DataLad, and the OpenNeuro CLI.