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590
datasets available to search
ShareScore release 0.9.0
Dataset results
590 results for “muscular dystrophies.”
Dose-Ranging Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy (DMD) Patients
ClinicalTrials.gov study NCT00844597. IPD Sharing: Not stated. Countries: 1. Publications: 1.
Clinical Trial to Evaluate the Efficacy, Safety, and Tolerability of RO7239361 in Ambulatory Boys With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03039686. IPD Sharing: Not stated. Countries: 13. Publications: 1.
A 5-year Natural History Study in LAMA2-related Muscular Dystrophy and SELENON-related Myopathy.
ClinicalTrials.gov study NCT06132750. IPD Sharing: UNDECIDED. Countries: 1. Publications: 1.
A Phase IIa Study of TAS-205 for Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT02752048. IPD Sharing: Not stated. Countries: 1. Publications: 1.
Clinical Intramuscular Gene Transfer of rAAV1.CMV.huFollistatin344 Trial to Patients With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT02354781. IPD Sharing: Not stated. Countries: 1. Publications: 5.
Finding the Optimum Regimen for Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT01603407. IPD Sharing: NO. Countries: 5. Publications: 58.
Safety and Efficacy of Pitolisant on Excessive Daytime Sleepiness and Other Non-Muscular Symptoms in Patients With Myotonic Dystrophy Type 1
ClinicalTrials.gov study NCT04886518. IPD Sharing: NO. Countries: 2. Publications: 1.
A Gene Transfer Therapy Study to Evaluate the Safety of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT03375164. IPD Sharing: Not stated. Countries: 1. Publications: 2.
A Clinical Study to Assess the Efficacy and Safety of GSK2402968 in Subjects With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT01254019. IPD Sharing: Not stated. Countries: 20. Publications: 1.
Efficacy and Safety of Losmapimod in Treating Subjects With Facioscapulohumeral Muscular Dystrophy (FSHD) With Open-Label Extension (OLE)
ClinicalTrials.gov study NCT04264442. IPD Sharing: NO. Countries: 4. Publications: 7.
Efficacy, Safety, and Tolerability Rollover Study of Eteplirsen in Subjects With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT01540409. IPD Sharing: Not stated. Countries: 1. Publications: 1.
Study of Ataluren for Previously Treated Participants With Nonsense Mutation Duchenne/Becker Muscular Dystrophy (nmDBMD) in Europe, Israel, Australia, and Canada
ClinicalTrials.gov study NCT01557400. IPD Sharing: NO. Countries: 10. Publications: 3.
Safety and Dose Finding Study of NS-065/NCNP-01 in Boys With Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT02740972. IPD Sharing: Not stated. Countries: 2. Publications: 1.
Phase 2B Extension Study of Ataluren (PTC124) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)
ClinicalTrials.gov study NCT00847379. IPD Sharing: NO. Countries: 11. Publications: 2.
Safety and Efficacy Study of Antisense Oligonucleotides in Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT00159250. IPD Sharing: Not stated. Countries: 1. Publications: 8.
Efficacy and Tolerability of Idebenone in Boys With Cardiac Dysfunction Associated With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT00654784. IPD Sharing: Not stated. Countries: 1. Publications: 1.
The Effect of Virtual Reality Applications on Upper Extremity Functions in Patients With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT07039799. IPD Sharing: NO. Countries: 0. Publications: 2.
Efficacy and Safety of Losmapimod in Subjects With Facioscapulohumeral Muscular Dystrophy (FSHD)
ClinicalTrials.gov study NCT04003974. IPD Sharing: NO. Countries: 4. Publications: 9.
Clinical Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT02851797. IPD Sharing: NO. Countries: 11. Publications: 1.
Study of Eteplirsen in Young Participants With Duchenne Muscular Dystrophy (DMD) Amenable to Exon 51 Skipping
ClinicalTrials.gov study NCT03218995. IPD Sharing: NO. Countries: 4. Publications: 1.
ScienceDex guides
Understand access before you commit
These curated guides explain access requirements, typical timelines, costs, and reuse considerations for widely used research datasets.
Allen Brain Atlas
Allen Brain Atlas is an Allen Institute collection of brain map atlases, datasets, APIs, and analysis tools covering mouse, human, and non-human primate brain resources.
Annotated Behaviour and Observability Dataset (ABODe)
ABODe is a University of Edinburgh DataShare dataset for behavior classification in group-housed mice using home-cage video, identities, bounding boxes, ground-plate positions, and annotator labels.
DANDI Archive for NWB datasets
DANDI is a BRAIN Initiative archive for publishing and sharing neurophysiology data, including electrophysiology, optophysiology, and behavioral data packaged as NWB and related standards.
International Brain Laboratory public data
The International Brain Laboratory public data releases expose standardized mouse decision-making experiments, including Neuropixels recordings, widefield calcium imaging, behavior, and session metadata accessed through the ONE API.
OpenNeuro
OpenNeuro is a free, open platform for sharing neuroimaging datasets, with public search, dataset pages, and download paths for web, S3, DataLad, and the OpenNeuro CLI.