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590
datasets available to search
ShareScore release 0.9.0
Dataset results
590 results for “muscular dystrophies.”
Natural History of Limb Girdle Muscular Dystrophy Type 2A and Type 2E
ClinicalTrials.gov study NCT03488784. IPD Sharing: NO. Countries: 1. Publications: 0.
Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Muscular Atrophy Identified by Newborn Screening
ClinicalTrials.gov study NCT07286565. IPD Sharing: NO. Countries: 1. Publications: 0.
Long-term Use of Viltolarsen in Boys With Duchenne Muscular Dystrophy in Clinical Practice (VILT-502)
ClinicalTrials.gov study NCT04687020. IPD Sharing: NO. Countries: 2. Publications: 0.
Phase IIb Study of PRO045 in Subjects With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT01826474. IPD Sharing: Not stated. Countries: 5. Publications: 0.
Phenotype - Genotype Correlation in a Sample of Egyptian Patients With Congenital Myopathies and Congenital Muscular Dystrophies
ClinicalTrials.gov study NCT07138963. IPD Sharing: YES. Countries: 1. Publications: 0.
Dual Task in Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT05575648. IPD Sharing: NO. Countries: 1. Publications: 0.
Evaluation of the Safety and Efficacy of BBM-D101 to Treat Patients with Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT06641895. IPD Sharing: NO. Countries: 1. Publications: 0.
Investigation Of Factors Affecting Hand Functions in Nonambulatory Patients With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03521271. IPD Sharing: UNDECIDED. Countries: 1. Publications: 0.
Extension Study of BMN 044 in Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT02958202. IPD Sharing: NO. Countries: 4. Publications: 0.
Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-251 in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping
ClinicalTrials.gov study NCT05524883. IPD Sharing: NO. Countries: 9. Publications: 0.
Effectiveness of 5-week Digital Respiratory Practice in Children With Duchenne and Becker Muscular Dystrophies.
ClinicalTrials.gov study NCT06363526. IPD Sharing: NO. Countries: 1. Publications: 0.
A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT07127978. IPD Sharing: NO. Countries: 1. Publications: 0.
Test-Retest Reliability of Pulmonary Function Tests in Patients With Duchenne's Muscular Dystrophy
ClinicalTrials.gov study NCT00207857. IPD Sharing: Not stated. Countries: 1. Publications: 0.
A Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT02251600. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Computerized Facial Recognition for Automated Diagnosis of the Facio-Scapulo-Humeral Muscular Dystrophy (FSMHD)
ClinicalTrials.gov study NCT04377217. IPD Sharing: NO. Countries: 1. Publications: 0.
Digestive Events in Duchenne Muscular Dystrophy Patients
ClinicalTrials.gov study NCT04384354. IPD Sharing: UNDECIDED. Countries: 1. Publications: 0.
Dietary Protein Requirements in Adults With Facioscapulohumeral Muscular Dystrophy
ClinicalTrials.gov study NCT06785428. IPD Sharing: Not stated. Countries: 1. Publications: 0.
AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT05693142. IPD Sharing: Not stated. Countries: 2. Publications: 0.
New Clinical Outcome Measures to Remotely Evaluate Patients With FacioScapuloHumeral Muscular Dystrophy
ClinicalTrials.gov study NCT05812144. IPD Sharing: NO. Countries: 1. Publications: 0.
Effect of Kinesiology Taping on Head and Trunk Control in Children With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT05967793. IPD Sharing: UNDECIDED. Countries: 1. Publications: 0.
ScienceDex guides
Understand access before you commit
These curated guides explain access requirements, typical timelines, costs, and reuse considerations for widely used research datasets.
Allen Brain Atlas
Allen Brain Atlas is an Allen Institute collection of brain map atlases, datasets, APIs, and analysis tools covering mouse, human, and non-human primate brain resources.
Annotated Behaviour and Observability Dataset (ABODe)
ABODe is a University of Edinburgh DataShare dataset for behavior classification in group-housed mice using home-cage video, identities, bounding boxes, ground-plate positions, and annotator labels.
DANDI Archive for NWB datasets
DANDI is a BRAIN Initiative archive for publishing and sharing neurophysiology data, including electrophysiology, optophysiology, and behavioral data packaged as NWB and related standards.
International Brain Laboratory public data
The International Brain Laboratory public data releases expose standardized mouse decision-making experiments, including Neuropixels recordings, widefield calcium imaging, behavior, and session metadata accessed through the ONE API.
OpenNeuro
OpenNeuro is a free, open platform for sharing neuroimaging datasets, with public search, dataset pages, and download paths for web, S3, DataLad, and the OpenNeuro CLI.