Find research datasets worth reusing
Search datasets from major research repositories and use ShareScore to quickly assess how well each record supports discovery, access, and reuse.
590
datasets available to search
ShareScore release 0.9.0
Dataset results
590 results for “muscular dystrophies.”
Phase III Study of Idebenone in Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT01027884. IPD Sharing: Not stated. Countries: 10. Publications: 2.
Weekly Steroids in Muscular Dystrophy
ClinicalTrials.gov study NCT04054375. IPD Sharing: NO. Countries: 1. Publications: 6.
Congenital Muscular Dystrophy Ascending Multiple Dose Cohort Study Analyzing Pharmacokinetics at Three Dose Levels In Children and Adolescents With Assessment of Safety and Tolerability of Omigapil (C
ClinicalTrials.gov study NCT01805024. IPD Sharing: Not stated. Countries: 1. Publications: 1.
Efficacy Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy Patients
ClinicalTrials.gov study NCT01396239. IPD Sharing: Not stated. Countries: 1. Publications: 2.
A Natural History Study In Chinese Male Patients With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03760029. IPD Sharing: NO. Countries: 1. Publications: 1.
Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03179631. IPD Sharing: NO. Countries: 18. Publications: 0.
Revatio for Heart Disease in Duchenne Muscular Dystrophy and Becker Muscular Dystrophy
ClinicalTrials.gov study NCT01168908. IPD Sharing: Not stated. Countries: 1. Publications: 1.
Long-term Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT03038399. IPD Sharing: Not stated. Countries: 6. Publications: 2.
A Study to Assess the Efficacy and Safety of Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT03439670. IPD Sharing: Not stated. Countries: 11. Publications: 44.
Historically Controlled Trial of Corticosteroids in Young Boys With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT02167217. IPD Sharing: Not stated. Countries: 1. Publications: 4.
Gene Transfer Clinical Trial to Deliver rAAVrh74.MCK.GALGT2 for Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03333590. IPD Sharing: Not stated. Countries: 1. Publications: 35.
Phase III Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03703882. IPD Sharing: Not stated. Countries: 8. Publications: 1.
A Study to Assess Vamorolone in Boys Ages 2 to <4 Years and 7 to <18 Years With Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT05185622. IPD Sharing: NO. Countries: 1. Publications: 22.
A Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT02760264. IPD Sharing: UNDECIDED. Countries: 6. Publications: 3.
Phase 2B Study of PTC124 (Ataluren) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)
ClinicalTrials.gov study NCT00592553. IPD Sharing: NO. Countries: 11. Publications: 3.
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT05096221. IPD Sharing: Not stated. Countries: 9. Publications: 5.
Oral Ifetroban in Subjects With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03340675. IPD Sharing: NO. Countries: 1. Publications: 1.
A Study of Tadalafil for Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT01865084. IPD Sharing: YES. Countries: 16. Publications: 3.
Novel DMD mouse model carrying a multi-exonic Dmd deletion exhibit progressive muscular dystrophy and early-onset cardiomyopathy
Open the record for dataset details and reuse information.
Data from: Epigenetic small molecule screening identifies a new HDACi compound for ameliorating Duchenne muscular dystrophy
Open the record for dataset details and reuse information.
ScienceDex guides
Understand access before you commit
These curated guides explain access requirements, typical timelines, costs, and reuse considerations for widely used research datasets.
Allen Brain Atlas
Allen Brain Atlas is an Allen Institute collection of brain map atlases, datasets, APIs, and analysis tools covering mouse, human, and non-human primate brain resources.
Annotated Behaviour and Observability Dataset (ABODe)
ABODe is a University of Edinburgh DataShare dataset for behavior classification in group-housed mice using home-cage video, identities, bounding boxes, ground-plate positions, and annotator labels.
DANDI Archive for NWB datasets
DANDI is a BRAIN Initiative archive for publishing and sharing neurophysiology data, including electrophysiology, optophysiology, and behavioral data packaged as NWB and related standards.
International Brain Laboratory public data
The International Brain Laboratory public data releases expose standardized mouse decision-making experiments, including Neuropixels recordings, widefield calcium imaging, behavior, and session metadata accessed through the ONE API.
OpenNeuro
OpenNeuro is a free, open platform for sharing neuroimaging datasets, with public search, dataset pages, and download paths for web, S3, DataLad, and the OpenNeuro CLI.