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87
datasets available to search
ShareScore release 0.9.0
Dataset results
87 results for “mucopolysaccharidosis”
Phase I/II Study of JR-441 in Patients With Mucopolysaccharidosis Type IIIA
ClinicalTrials.gov study NCT06095388. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Dynamic Gait Analysis in Children With Mucopolysaccharidosis Type IVa
ClinicalTrials.gov study NCT02153255. IPD Sharing: Not stated. Countries: 1. Publications: 0.
An Extension Study of JR-141-BR21 in Patients With Mucopolysaccharidosis II
ClinicalTrials.gov study NCT03708965. IPD Sharing: NO. Countries: 1. Publications: 0.
An Extension Study of JR-171-101 Study in Patients With Mucopolysaccharidosis Type I (MPS I)
ClinicalTrials.gov study NCT04453085. IPD Sharing: NO. Countries: 3. Publications: 0.
Natural History Study to Characterise the Course of Disease Progression in Participants With Mucopolysaccharidosis Type IIIB
ClinicalTrials.gov study NCT02293408. IPD Sharing: Not stated. Countries: 6. Publications: 0.
A Study of JR-141 in Patients With Mucopolysaccharidosis II (BR21)
ClinicalTrials.gov study NCT03359213. IPD Sharing: NO. Countries: 1. Publications: 0.
A Study of JR-141 in Patients With Mucopolysaccharidosis II
ClinicalTrials.gov study NCT03568175. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Study of DNL126 in Pediatric Participants With Mucopolysaccharidosis Type IIIA (Sanfilippo Syndrome Type A)
ClinicalTrials.gov study NCT06181136. IPD Sharing: NO. Countries: 1. Publications: 0.
Intrathecal Enzyme Replacement Therapy for Spinal Cord Compression in Mucopolysaccharidosis (MPS) I
ClinicalTrials.gov study NCT00215527. IPD Sharing: Not stated. Countries: 2. Publications: 0.
A Multi-cohort Study of Safety, Efficacy, PK and PD of GNR-055 in Patients With Mucopolysaccharidosis Type II
ClinicalTrials.gov study NCT05208281. IPD Sharing: NO. Countries: 1. Publications: 0.
A Study of ELAPRASE in Treatment-naïve Participants With Hunter Syndrome (Mucopolysaccharidosis [MPS] II)
ClinicalTrials.gov study NCT05494593. IPD Sharing: NO. Countries: 1. Publications: 0.
Hematopoietic Stem Cell Transplantation for Mucopolysaccharidosis
ClinicalTrials.gov study NCT01238328. IPD Sharing: Not stated. Countries: 1. Publications: 0.
An Extension Study of JR-141 in Patients With Mucopolysaccharidosis Type II
ClinicalTrials.gov study NCT04348136. IPD Sharing: Not stated. Countries: 1. Publications: 0.
A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of JWK008 in Patients With Mucopolysaccharidosis Type I
ClinicalTrials.gov study NCT06519552. IPD Sharing: NO. Countries: 1. Publications: 0.
Gene Therapy with Modified Autologous Hematopoietic Stem Cells for Patients with Mucopolysaccharidosis Type II
ClinicalTrials.gov study NCT05665166. IPD Sharing: NO. Countries: 1. Publications: 0.
Ultrasound Findings of Finger, Wrist and Knee Joints in Mucopolysaccharidosis
ClinicalTrials.gov study NCT02067650. IPD Sharing: Not stated. Countries: 1. Publications: 0.
The Long-term Safety Study of Idursulfase-beta in Hunter Syndrome(Mucopolysaccharidosis II) Patients
ClinicalTrials.gov study NCT02044692. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Core Outcome Set for Head, Neck and Respiratory Disease in Mucopolysaccharidosis II
ClinicalTrials.gov study NCT06022380. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Diagnosis of Mucopolysaccharidosis Disorders in Patients Presenting With Bilateral Hip Disease
ClinicalTrials.gov study NCT01707433. IPD Sharing: Not stated. Countries: 1. Publications: 0.
Mucopolysaccharidosis VII Disease Monitoring Program
ClinicalTrials.gov study NCT03604835. IPD Sharing: Not stated. Countries: 8. Publications: 0.
ScienceDex guides
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Allen Brain Atlas
Allen Brain Atlas is an Allen Institute collection of brain map atlases, datasets, APIs, and analysis tools covering mouse, human, and non-human primate brain resources.
Annotated Behaviour and Observability Dataset (ABODe)
ABODe is a University of Edinburgh DataShare dataset for behavior classification in group-housed mice using home-cage video, identities, bounding boxes, ground-plate positions, and annotator labels.
DANDI Archive for NWB datasets
DANDI is a BRAIN Initiative archive for publishing and sharing neurophysiology data, including electrophysiology, optophysiology, and behavioral data packaged as NWB and related standards.
International Brain Laboratory public data
The International Brain Laboratory public data releases expose standardized mouse decision-making experiments, including Neuropixels recordings, widefield calcium imaging, behavior, and session metadata accessed through the ONE API.
OpenNeuro
OpenNeuro is a free, open platform for sharing neuroimaging datasets, with public search, dataset pages, and download paths for web, S3, DataLad, and the OpenNeuro CLI.