Dataset related to the article "Complete phenotype rescue through the restoration of full-length dystrophin using CRISPR/Cas9 genome editing in Duchenne muscular dystrophy patient-derived iPSCs carrying the deletion of two exons."

<p><span>This record contains raw data related to the article Dataset related to the article &ldquo;Complete phenotype rescue through the restoration of full-length dystrophin using CRISPR/Cas9 genome editing in Duchenne muscular dystrophy patient-derived iPSCs carrying the deletion of two exons".</span></p> <p><span>Here we describe for the first time the restoration of the full-length dystrophin protein, by CRISPR/Cas9, in an iPSC derived from a Duchenne patient carrying the deletion of two exons, allowing the recovery of the cardiac pathological phenotypes and mechanisms, as assessed from the transcriptional, structural, and functional point of view.</span></p>