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ClinicalTrials.govrestricted

Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease

ClinicalTrials.gov study NCT01230801. IPD Sharing: Not stated. Countries: 5. Publications: 0.

ShareScore

28/100

Overall dataset sharing score

Score breakdown

These five areas show where the dataset supports — or may limit — practical reuse.

Stewardship
12
Harmonization
8
Access
4
Reuse readiness
0
Engagement
4

Topics