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1,336 results for “congenital”

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ClinicalTrials.gov36/100

Global Safety and Efficacy Registration Study of Crinecerfont for Congenital Adrenal Hyperplasia

ClinicalTrials.gov study NCT04490915. IPD Sharing: NO. Countries: 18. Publications: 1.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov36/100

Subcutaneous Hydrocortisone Children With Congenital Adrenal Hyperplasia

ClinicalTrials.gov study NCT03718234. IPD Sharing: NO. Countries: 1. Publications: 1.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov36/100

Phase III Study of Coagulation FVIIa (Recombinant) in Congenital Hemophilia A or B Patients With Inhibitors

ClinicalTrials.gov study NCT02020369. IPD Sharing: NO. Countries: 10. Publications: 2.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov36/100

Donor Stem Cell Transplantation for Congenital Immunodeficiencies

ClinicalTrials.gov study NCT00426517. IPD Sharing: NO. Countries: 1. Publications: 6.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov36/100

Pharmacokinetic, Efficacy and Safety of BT524 in Patients With Congenital Fibrinogen Deficiency

ClinicalTrials.gov study NCT02065882. IPD Sharing: NO. Countries: 5. Publications: 0.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov36/100

A Study of TAK-662 for Japanese Patients With Congenital Protein C Deficiency

ClinicalTrials.gov study NCT04984889. IPD Sharing: NO. Countries: 1. Publications: 0.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov36/100

Specialized Pacing for Patients With Congenital Heart Disease

ClinicalTrials.gov study NCT03361189. IPD Sharing: NO. Countries: 1. Publications: 10.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov36/100

A Study of ATR-101 for the Treatment of Congenital Adrenal Hyperplasia

ClinicalTrials.gov study NCT02804178. IPD Sharing: NO. Countries: 1. Publications: 1.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov36/100

N-Acetylcysteine in Neonatal Congenital Heart Surgery (INACT Study)

ClinicalTrials.gov study NCT00374088. IPD Sharing: Not stated. Countries: 1. Publications: 15.

restrictedIPD-UNDECIDEDFeb 2026View details →
ClinicalTrials.gov36/100

Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of NBI-74788 in Adults With Congenital Adrenal Hyperplasia

ClinicalTrials.gov study NCT03525886. IPD Sharing: NO. Countries: 1. Publications: 1.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov36/100

A Study of the Safety and Pharmacokinetics of Apixaban Versus Vitamin K Antagonist (VKA) or Low Molecular Weight Heparin (LMWH) in Pediatric Subjects With Congenital or Acquired Heart Disease Requirin

ClinicalTrials.gov study NCT02981472. IPD Sharing: Not stated. Countries: 14. Publications: 1.

restrictedIPD-UNDECIDEDFeb 2026View details →
ClinicalTrials.gov36/100

Valganciclovir Therapy in Infants and Children With Congenital CMV Infection and Hearing Loss

ClinicalTrials.gov study NCT01649869. IPD Sharing: Not stated. Countries: 2. Publications: 1.

restrictedIPD-UNDECIDEDFeb 2026View details →
ClinicalTrials.gov36/100

Phase 1/2 Safety and Efficacy Study of AAV-RPE65 Vector to Treat Leber Congenital Amaurosis

ClinicalTrials.gov study NCT00749957. IPD Sharing: Not stated. Countries: 1. Publications: 5.

restrictedIPD-UNDECIDEDFeb 2026View details →
ClinicalTrials.gov36/100

Short-Term vs. Long-Term Valganciclovir Therapy for Symptomatic Congenital CMV Infections

ClinicalTrials.gov study NCT00466817. IPD Sharing: Not stated. Countries: 2. Publications: 1.

restrictedIPD-UNDECIDEDFeb 2026View details →
ClinicalTrials.gov36/100

The Pharmacology and Hemodynamics of Dexmedetomidine in Children With Congenital Heart Disease

ClinicalTrials.gov study NCT00480740. IPD Sharing: Not stated. Countries: 1. Publications: 2.

restrictedIPD-UNDECIDEDFeb 2026View details →
ClinicalTrials.gov36/100

Improving the Results of Bone Marrow Transplantation for Patients With Severe Congenital Anemias

ClinicalTrials.gov study NCT00061568. IPD Sharing: YES. Countries: 1. Publications: 7.

controlledIPD-YESFeb 2026View details →
ClinicalTrials.gov36/100

Pharmacologic Treatment of Congenital Nephrogenic Diabetes Insipidus

ClinicalTrials.gov study NCT00478335. IPD Sharing: NO. Countries: 2. Publications: 8.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov36/100

Congenital Muscular Dystrophy Ascending Multiple Dose Cohort Study Analyzing Pharmacokinetics at Three Dose Levels In Children and Adolescents With Assessment of Safety and Tolerability of Omigapil (C

ClinicalTrials.gov study NCT01805024. IPD Sharing: Not stated. Countries: 1. Publications: 1.

restrictedIPD-UNDECIDEDFeb 2026View details →
ClinicalTrials.gov36/100

Safety of a Single Intravenous Dose of Recombinant Factor XIII in Children With Congenital FXIII A-subunit Deficiency

ClinicalTrials.gov study NCT01230021. IPD Sharing: Not stated. Countries: 3. Publications: 2.

restrictedIPD-UNDECIDEDFeb 2026View details →
ClinicalTrials.gov36/100

Milrinone in Congenital Diaphragmatic Hernia

ClinicalTrials.gov study NCT02951130. IPD Sharing: YES. Countries: 1. Publications: 1.

controlledIPD-YESFeb 2026View details →

ScienceDex guides

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These curated guides explain access requirements, typical timelines, costs, and reuse considerations for widely used research datasets.

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Allen Brain Atlas

Allen Brain Atlas is an Allen Institute collection of brain map atlases, datasets, APIs, and analysis tools covering mouse, human, and non-human primate brain resources.

allen-brain-atlas
neuroscienceopenDocumentation, web resources, and API references are available online.
Last verified 2026-04-30Open record

Annotated Behaviour and Observability Dataset (ABODe)

ABODe is a University of Edinburgh DataShare dataset for behavior classification in group-housed mice using home-cage video, identities, bounding boxes, ground-plate positions, and annotator labels.

abode-home-cage
behavioral-neuroscienceopenThe DataShare record exposes download links for annotations, documentation, license text, and the zipped per-snippet data directory.
Last verified 2026-04-30Open record

DANDI Archive for NWB datasets

DANDI is a BRAIN Initiative archive for publishing and sharing neurophysiology data, including electrophysiology, optophysiology, and behavioral data packaged as NWB and related standards.

dandi-nwb
electrophysiologyopenPublished Dandiset metadata and archive endpoints are available through the production DANDI API.
Last verified 2026-04-30Open record

International Brain Laboratory public data

The International Brain Laboratory public data releases expose standardized mouse decision-making experiments, including Neuropixels recordings, widefield calcium imaging, behavior, and session metadata accessed through the ONE API.

ibl
behavioral-neuroscienceopenPublic sessions can be searched and loaded from the IBL public data server through ONE.
Last verified 2026-04-29Open record

OpenNeuro

OpenNeuro is a free, open platform for sharing neuroimaging datasets, with public search, dataset pages, and download paths for web, S3, DataLad, and the OpenNeuro CLI.

openneuro
neuroscienceopenPublished datasets are available on demand over the internet.
Last verified 2026-04-29Open record