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89 results for “pnh”

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ClinicalTrials.gov28/100

A Study to Evaluate How Safe Pozelimab + Cemdisiran Combination Therapy is and How Well it Works in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Who Have Not Recently Received or Have

ClinicalTrials.gov study NCT05133531. IPD Sharing: YES. Countries: 24. Publications: 0.

controlledIPD-YESFeb 2026View details →
ClinicalTrials.gov28/100

BCX9930 for the Treatment of Paroxysmal Nocturnal Hemoglobinuria (PNH) in Participants Not Receiving Other Complement Inhibitor Therapy

ClinicalTrials.gov study NCT05116787. IPD Sharing: NO. Countries: 3. Publications: 0.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov28/100

Study to Evaluate the Efficacy and Safety of REGN3918 in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

ClinicalTrials.gov study NCT03946748. IPD Sharing: YES. Countries: 5. Publications: 0.

controlledIPD-YESFeb 2026View details →
ClinicalTrials.gov28/100

Coversin in PNH in Patients With Resistance to Eculizumab Due to Complement C5 Polymorphisms

ClinicalTrials.gov study NCT03427060. IPD Sharing: Not stated. Countries: 1. Publications: 0.

restrictedIPD-UNDECIDEDFeb 2026View details →
ClinicalTrials.gov28/100

Phase 2 Safety and Efficacy Study of Zilucoplan (RA101495) to Treat PNH Patients

ClinicalTrials.gov study NCT03078582. IPD Sharing: NO. Countries: 8. Publications: 0.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov28/100

Efficacy, Safety, Pharmacokinetics, Pharmacodynamics, and Immunogenicity of Ravulizumab in Chinese Adults Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH)

ClinicalTrials.gov study NCT06578949. IPD Sharing: YES. Countries: 1. Publications: 0.

controlledIPD-YESFeb 2026View details →
ClinicalTrials.gov28/100

Eculizumab in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) in China

ClinicalTrials.gov study NCT05886244. IPD Sharing: YES. Countries: 1. Publications: 0.

controlledIPD-YESFeb 2026View details →
ClinicalTrials.gov28/100

Phase 2 Safety and Efficacy Study of Zilucoplan (RA101495) to Treat PNH Patients Who Have an Inadequate Response to Eculizumab

ClinicalTrials.gov study NCT03030183. IPD Sharing: Not stated. Countries: 1. Publications: 0.

restrictedIPD-UNDECIDEDFeb 2026View details →
geo24/100

Whole transcriptome sequencing identifies increased CXCR2 expression in PNH granulocytes

GEO Series GSE80062. Homo sapiens. 7 samples. Type: Expression profiling by high throughput sequencing.

openGEO-OpenApr 2016View details →
ClinicalTrials.gov24/100

Safety and Pharmacokinetics of TT30 in Subjects With Paroxysmal Nocturnal Hemoglobinuria (PNH)

ClinicalTrials.gov study NCT01335165. IPD Sharing: Not stated. Countries: 5. Publications: 0.

restrictedIPD-UNDECIDEDFeb 2026View details →
ClinicalTrials.gov24/100

Study of Danicopan as Add-on Treatment to Ravulizumab or Eculizumab in Pediatric Participants With PNH Who Have Clinically Significant Extravascular Hemolysis

ClinicalTrials.gov study NCT06449001. IPD Sharing: YES. Countries: 3. Publications: 0.

controlledIPD-YESFeb 2026View details →
ClinicalTrials.gov24/100

Efficacy, Safety, and Pharmacokinetics of LP-005 Injection in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

ClinicalTrials.gov study NCT07266155. IPD Sharing: Not stated. Countries: 1. Publications: 0.

restrictedIPD-UNDECIDEDFeb 2026View details →
ClinicalTrials.gov24/100

Dose Escalation of BCX10013 in Participants with Paroxysmal Nocturnal Hemoglobinuria (PNH)

ClinicalTrials.gov study NCT06100900. IPD Sharing: NO. Countries: 2. Publications: 0.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov24/100

Real-life Treatment Outcomes of Ravulizumab in PNH

ClinicalTrials.gov study NCT06633536. IPD Sharing: YES. Countries: 1. Publications: 0.

controlledIPD-YESFeb 2026View details →
ClinicalTrials.gov24/100

A Study to Evaluate the Efficacy and Safety of HSK39297 in Patients With Paroxysmal Nocturnal Hemoglobinuria(PNH)

ClinicalTrials.gov study NCT06561841. IPD Sharing: NO. Countries: 1. Publications: 0.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov24/100

A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Preliminary Efficacy of of VSA012 in Subjects with Paroxysmal Nocturnal Hemoglobinuria(PNH)

ClinicalTrials.gov study NCT06848296. IPD Sharing: NO. Countries: 0. Publications: 0.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov24/100

Home Reported Outcomes in PNH

ClinicalTrials.gov study NCT06411626. IPD Sharing: NO. Countries: 1. Publications: 0.

closedIPD-NOFeb 2026View details →
ClinicalTrials.gov24/100

A Long-term Safety and Efficacy Study of Danicopan as an Add-on Therapy to Complement Component 5 Inhibitor (C5i) in Participants With PNH

ClinicalTrials.gov study NCT05389449. IPD Sharing: YES. Countries: 15. Publications: 0.

controlledIPD-YESFeb 2026View details →
ClinicalTrials.gov24/100

Efficacy, Safety, and Pharmacokinetics of LP-005 Injection in PNH Patients.

ClinicalTrials.gov study NCT07212426. IPD Sharing: Not stated. Countries: 1. Publications: 0.

restrictedIPD-UNDECIDEDFeb 2026View details →
ClinicalTrials.gov24/100

Global PNH Patient Registry

ClinicalTrials.gov study NCT05755867. IPD Sharing: YES. Countries: 1. Publications: 0.

controlledIPD-YESFeb 2026View details →

ScienceDex guides

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Allen Brain Atlas

Allen Brain Atlas is an Allen Institute collection of brain map atlases, datasets, APIs, and analysis tools covering mouse, human, and non-human primate brain resources.

allen-brain-atlas
neuroscienceopenDocumentation, web resources, and API references are available online.
Last verified 2026-04-30Open record

Annotated Behaviour and Observability Dataset (ABODe)

ABODe is a University of Edinburgh DataShare dataset for behavior classification in group-housed mice using home-cage video, identities, bounding boxes, ground-plate positions, and annotator labels.

abode-home-cage
behavioral-neuroscienceopenThe DataShare record exposes download links for annotations, documentation, license text, and the zipped per-snippet data directory.
Last verified 2026-04-30Open record

DANDI Archive for NWB datasets

DANDI is a BRAIN Initiative archive for publishing and sharing neurophysiology data, including electrophysiology, optophysiology, and behavioral data packaged as NWB and related standards.

dandi-nwb
electrophysiologyopenPublished Dandiset metadata and archive endpoints are available through the production DANDI API.
Last verified 2026-04-30Open record

International Brain Laboratory public data

The International Brain Laboratory public data releases expose standardized mouse decision-making experiments, including Neuropixels recordings, widefield calcium imaging, behavior, and session metadata accessed through the ONE API.

ibl
behavioral-neuroscienceopenPublic sessions can be searched and loaded from the IBL public data server through ONE.
Last verified 2026-04-29Open record

OpenNeuro

OpenNeuro is a free, open platform for sharing neuroimaging datasets, with public search, dataset pages, and download paths for web, S3, DataLad, and the OpenNeuro CLI.

openneuro
neuroscienceopenPublished datasets are available on demand over the internet.
Last verified 2026-04-29Open record