Find research datasets worth reusing
Search datasets from major research repositories and use ShareScore to quickly assess how well each record supports discovery, access, and reuse.
826
datasets available to search
ShareScore release 0.9.0
Dataset results
826 results for “gene therapy”
Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy
ClinicalTrials.gov study NCT02559830. IPD Sharing: Not stated. Countries: 1. Publications: 5.
Repeated Application of Gene Therapy in CF Patients
ClinicalTrials.gov study NCT01621867. IPD Sharing: Not stated. Countries: 1. Publications: 3.
Cystic Fibrosis (CF) Leukocyte Genes as Biomarkers for Novel Therapies
ClinicalTrials.gov study NCT00727285. IPD Sharing: Not stated. Countries: 1. Publications: 1.
Gene Therapy for Chinese Hemophilia B
ClinicalTrials.gov study NCT04135300. IPD Sharing: YES. Countries: 1. Publications: 1.
Safety and Efficacy of GS-100 Gene Therapy in Patients With NGLY1 Deficiency
ClinicalTrials.gov study NCT06199531. IPD Sharing: NO. Countries: 1. Publications: 3.
Gene Therapy for Transfusion Dependent Beta-thalassemia
ClinicalTrials.gov study NCT02453477. IPD Sharing: Not stated. Countries: 1. Publications: 8.
A Fabry Disease Gene Therapy Study
ClinicalTrials.gov study NCT04040049. IPD Sharing: Not stated. Countries: 7. Publications: 1.
PDE6A Gene Therapy for Retinitis Pigmentosa
ClinicalTrials.gov study NCT04611503. IPD Sharing: Not stated. Countries: 1. Publications: 1.
Intracerebral Gene Therapy in Children With Sanfilippo Type B Syndrome
ClinicalTrials.gov study NCT03300453. IPD Sharing: Not stated. Countries: 1. Publications: 1.
Epicardial Delivery of XC001 Gene Therapy for Refractory Angina Coronary Treatment (The EXACT Trial)
ClinicalTrials.gov study NCT04125732. IPD Sharing: NO. Countries: 1. Publications: 4.
Gene Therapy for Netherton Syndrome
ClinicalTrials.gov study NCT01545323. IPD Sharing: Not stated. Countries: 1. Publications: 3.
Safety and Efficacy Trial of AAV Gene Therapy in Patients With CNGB3 Achromatopsia (A Clarity Clinical Trial)
ClinicalTrials.gov study NCT02599922. IPD Sharing: Not stated. Countries: 1. Publications: 2.
NGGT006 Gene Therapy for Homozygous Familial Hypercholesterolemia
ClinicalTrials.gov study NCT06125847. IPD Sharing: NO. Countries: 1. Publications: 0.
Evaluation of the Safety and Efficacy of Hemophilia B Gene Therapy Drug
ClinicalTrials.gov study NCT05203679. IPD Sharing: NO. Countries: 1. Publications: 1.
Study to Evaluate the Safety of a Gene and Cell Therapy Product in Participants With HIV That is Well-Controlled on Antiretroviral Therapy
ClinicalTrials.gov study NCT04561258. IPD Sharing: UNDECIDED. Countries: 1. Publications: 1.
Intracerebral Gene Therapy for Children With Early Onset Forms of Metachromatic Leukodystrophy
ClinicalTrials.gov study NCT01801709. IPD Sharing: Not stated. Countries: 1. Publications: 5.
First-in-Human Study of TSHA-101 Gene Therapy for Treatment of Infantile Onset GM2 Gangliosidosis
ClinicalTrials.gov study NCT04798235. IPD Sharing: NO. Countries: 1. Publications: 1.
Safety Study of AADC Gene Therapy (VY-AADC01) for Parkinson's Disease
ClinicalTrials.gov study NCT01973543. IPD Sharing: UNDECIDED. Countries: 1. Publications: 2.
Gene Therapy for Chinese Hemophilia A
ClinicalTrials.gov study NCT04728841. IPD Sharing: NO. Countries: 1. Publications: 0.
Gene Therapy with Modified Autologous Hematopoietic Stem Cells for Patients with Mucopolysaccharidosis Type IIIA
ClinicalTrials.gov study NCT04201405. IPD Sharing: NO. Countries: 1. Publications: 5.
ScienceDex guides
Understand access before you commit
These curated guides explain access requirements, typical timelines, costs, and reuse considerations for widely used research datasets.
Allen Brain Atlas
Allen Brain Atlas is an Allen Institute collection of brain map atlases, datasets, APIs, and analysis tools covering mouse, human, and non-human primate brain resources.
Annotated Behaviour and Observability Dataset (ABODe)
ABODe is a University of Edinburgh DataShare dataset for behavior classification in group-housed mice using home-cage video, identities, bounding boxes, ground-plate positions, and annotator labels.
DANDI Archive for NWB datasets
DANDI is a BRAIN Initiative archive for publishing and sharing neurophysiology data, including electrophysiology, optophysiology, and behavioral data packaged as NWB and related standards.
International Brain Laboratory public data
The International Brain Laboratory public data releases expose standardized mouse decision-making experiments, including Neuropixels recordings, widefield calcium imaging, behavior, and session metadata accessed through the ONE API.
OpenNeuro
OpenNeuro is a free, open platform for sharing neuroimaging datasets, with public search, dataset pages, and download paths for web, S3, DataLad, and the OpenNeuro CLI.