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343
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ShareScore release 0.9.0
Dataset results
343 results for “Duchenne muscular dystrophy”
Multiomics Analysis of the mdx/mTR Mouse Model of Duchenne Muscular Dystrophy
<p>This dataset contains RNA sequencing, proteomics, metabolomics, lipidomics, primer sequence, and Ingenuity Pathway Analysis data for a study evaluating differences between the transcriptome, proteome, metabolome, and lipidome of lower limb muscles of mdx/mTR (Jackson Labs strain 023535) and wild-type C57BL/6J (Jackson Labs strain 000664) mice. Updated from previous submission, DOI: 10.5281/zenodo.3370799.</p>
Phase 3 Study of Ataluren in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)
ClinicalTrials.gov study NCT01826487. IPD Sharing: NO. Countries: 18. Publications: 4.
Trial of Pamrevlumab (FG-3019), in Non-Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT02606136. IPD Sharing: UNDECIDED. Countries: 1. Publications: 1.
Study to Evaluate the Safety and Efficacy of PF-06939926 for the Treatment of Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT04281485. IPD Sharing: YES. Countries: 15. Publications: 0.
An Open-label Extension Study To Evaluate Safety Of PF-06252616 In Boys With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT02907619. IPD Sharing: YES. Countries: 5. Publications: 1.
A Phase 2 Study to Evaluate the Safety, Efficacy, Pharmacokinetics and Pharmacodynamics of PF-06252616 in Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT02310763. IPD Sharing: YES. Countries: 8. Publications: 8.
A Study of CAP-1002 in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03406780. IPD Sharing: NO. Countries: 1. Publications: 1.
Eplerenone for Subclinical Cardiomyopathy in Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT01521546. IPD Sharing: Not stated. Countries: 1. Publications: 2.
An Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT02760277. IPD Sharing: Not stated. Countries: 6. Publications: 3.
Therapeutic Potential for Aldosterone Inhibition in Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT02354352. IPD Sharing: NO. Countries: 1. Publications: 1.
A Study to Evaluate the Safety and Tolerability of PF-06939926 Gene Therapy in Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03362502. IPD Sharing: NO. Countries: 1. Publications: 4.
Phase 2a Extension Study of Ataluren (PTC124) in Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT00759876. IPD Sharing: NO. Countries: 1. Publications: 2.
Outcome Measures in Duchenne Muscular Dystrophy: A Natural History Study
ClinicalTrials.gov study NCT02780492. IPD Sharing: YES. Countries: 3. Publications: 3.
A Randomized, Double-blind, Placebo-controlled Study of Delandistrogene Moxeparvovec (SRP-9001) for Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT03769116. IPD Sharing: Not stated. Countries: 1. Publications: 1.
Dose-Ranging Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy (DMD) Patients
ClinicalTrials.gov study NCT00844597. IPD Sharing: Not stated. Countries: 1. Publications: 1.
Clinical Trial to Evaluate the Efficacy, Safety, and Tolerability of RO7239361 in Ambulatory Boys With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT03039686. IPD Sharing: Not stated. Countries: 13. Publications: 1.
A Phase IIa Study of TAS-205 for Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT02752048. IPD Sharing: Not stated. Countries: 1. Publications: 1.
Clinical Intramuscular Gene Transfer of rAAV1.CMV.huFollistatin344 Trial to Patients With Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT02354781. IPD Sharing: Not stated. Countries: 1. Publications: 5.
Finding the Optimum Regimen for Duchenne Muscular Dystrophy
ClinicalTrials.gov study NCT01603407. IPD Sharing: NO. Countries: 5. Publications: 58.
A Gene Transfer Therapy Study to Evaluate the Safety of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)
ClinicalTrials.gov study NCT03375164. IPD Sharing: Not stated. Countries: 1. Publications: 2.
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Allen Brain Atlas
Allen Brain Atlas is an Allen Institute collection of brain map atlases, datasets, APIs, and analysis tools covering mouse, human, and non-human primate brain resources.
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DANDI Archive for NWB datasets
DANDI is a BRAIN Initiative archive for publishing and sharing neurophysiology data, including electrophysiology, optophysiology, and behavioral data packaged as NWB and related standards.
International Brain Laboratory public data
The International Brain Laboratory public data releases expose standardized mouse decision-making experiments, including Neuropixels recordings, widefield calcium imaging, behavior, and session metadata accessed through the ONE API.
OpenNeuro
OpenNeuro is a free, open platform for sharing neuroimaging datasets, with public search, dataset pages, and download paths for web, S3, DataLad, and the OpenNeuro CLI.