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89
datasets available to search
ShareScore release 0.9.0
Dataset results
89 results for “pnh”
Study of Efficacy and Safety of Twice Daily Oral LNP023 in Adult PNH Patients With Residual Anemia Despite Anti-C5 Antibody Treatment
ClinicalTrials.gov study NCT04558918. IPD Sharing: YES. Countries: 12. Publications: 3.
Study of Efficacy and Safety of Twice Daily Oral Iptacopan (LNP023) in Adult PNH Patients Who Are Naive to Complement Inhibitor Therapy
ClinicalTrials.gov study NCT04820530. IPD Sharing: YES. Countries: 8. Publications: 3.
Study of Safety, Efficacy, Tolerability, Pharmacokinetics and Pharmacodynamics of LNP023 in in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)
ClinicalTrials.gov study NCT03439839. IPD Sharing: YES. Countries: 3. Publications: 1.
A Study Evaluating the Efficacy and Safety of ABP 959 Compared With Eculizumab in Adult Participants With PNH
ClinicalTrials.gov study NCT03818607. IPD Sharing: YES. Countries: 14. Publications: 1.
A Study Evaluating the Efficacy and Safety of Crovalimab Versus Eculizumab in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) Not Previously Treated With Complement Inhibitors
ClinicalTrials.gov study NCT04434092. IPD Sharing: YES. Countries: 23. Publications: 2.
Extension Study of RA101495 for Patients With PNH Who Have Completed a Zilucoplan (RA101495) Clinical Study
ClinicalTrials.gov study NCT03225287. IPD Sharing: YES. Countries: 8. Publications: 1.
Ravulizumab Subcutaneous (SC) Versus Ravulizumab Intravenous (IV) in Adults With Paroxysmal Nocturnal Hemoglobinuria (PNH) Currently Treated With Eculizumab
ClinicalTrials.gov study NCT03748823. IPD Sharing: NO. Countries: 14. Publications: 1.
Danicopan as Add-on Therapy to a C5 Inhibitor in Paroxysmal Nocturnal Hemoglobinuria (PNH) Participants Who Have Clinically Evident Extravascular Hemolysis (EVH)(ALPHA)
ClinicalTrials.gov study NCT04469465. IPD Sharing: Not stated. Countries: 18. Publications: 2.
ALXN1210 (Ravulizumab) Versus Eculizumab in Complement Inhibitor Treatment-Naïve Adult Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH)
ClinicalTrials.gov study NCT02946463. IPD Sharing: Not stated. Countries: 26. Publications: 6.
Dose-Escalation Study of ALXN1210 IV in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH)
ClinicalTrials.gov study NCT02598583. IPD Sharing: YES. Countries: 2. Publications: 1.
A Study Evaluating the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of Crovalimab in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) Not Previously Treated With Complement Inhib
ClinicalTrials.gov study NCT04654468. IPD Sharing: YES. Countries: 1. Publications: 2.
Study of the Oral Factor D (FD) Inhibitor ALXN2050 in PNH Patients as Monotherapy
ClinicalTrials.gov study NCT04170023. IPD Sharing: YES. Countries: 7. Publications: 1.
Open-label, Multiple Ascending Dose Study of Ravulizumab (ALXN1210) in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH)
ClinicalTrials.gov study NCT02605993. IPD Sharing: Not stated. Countries: 7. Publications: 1.
Eculizumab Pharmacokinetics/Pharmacodynamics Study in Pediatric/Adolescent Paroxysmal Nocturnal Hemoglobinuria (PNH)
ClinicalTrials.gov study NCT00867932. IPD Sharing: Not stated. Countries: 1. Publications: 1.
Extension Study of Eculizumab in Patients With Transfusion Dependent Paroxysmal Nocturnal Hemoglobinuria (PNH)
ClinicalTrials.gov study NCT00122317. IPD Sharing: NO. Countries: 12. Publications: 1.
Pilot Study to Assess Safety, Preliminary Efficacy and Pharmacokinetics of S.C. Pegcetacoplan (APL-2) in PNH Subjects.
ClinicalTrials.gov study NCT02588833. IPD Sharing: Not stated. Countries: 4. Publications: 2.
ALXN1210 Versus Eculizumab in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) Currently Treated With Eculizumab
ClinicalTrials.gov study NCT03056040. IPD Sharing: Not stated. Countries: 11. Publications: 9.
A Phase IIa Study to Assess the Safety, Efficacy, and Pharmacokinetics of Subcutaneously Administered Pegcetacoplan (APL-2) in Subjects With PNH
ClinicalTrials.gov study NCT03593200. IPD Sharing: Not stated. Countries: 2. Publications: 1.
Study of Danicopan in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH)
ClinicalTrials.gov study NCT03053102. IPD Sharing: Not stated. Countries: 4. Publications: 1.
Coversin in Paroxysmal Nocturnal Haemoglobinuria (PNH)
ClinicalTrials.gov study NCT02591862. IPD Sharing: Not stated. Countries: 1. Publications: 1.
ScienceDex guides
Understand access before you commit
These curated guides explain access requirements, typical timelines, costs, and reuse considerations for widely used research datasets.
Allen Brain Atlas
Allen Brain Atlas is an Allen Institute collection of brain map atlases, datasets, APIs, and analysis tools covering mouse, human, and non-human primate brain resources.
Annotated Behaviour and Observability Dataset (ABODe)
ABODe is a University of Edinburgh DataShare dataset for behavior classification in group-housed mice using home-cage video, identities, bounding boxes, ground-plate positions, and annotator labels.
DANDI Archive for NWB datasets
DANDI is a BRAIN Initiative archive for publishing and sharing neurophysiology data, including electrophysiology, optophysiology, and behavioral data packaged as NWB and related standards.
International Brain Laboratory public data
The International Brain Laboratory public data releases expose standardized mouse decision-making experiments, including Neuropixels recordings, widefield calcium imaging, behavior, and session metadata accessed through the ONE API.
OpenNeuro
OpenNeuro is a free, open platform for sharing neuroimaging datasets, with public search, dataset pages, and download paths for web, S3, DataLad, and the OpenNeuro CLI.