The notices it replaced
- Reissues: PAR-22-030 Translational Efforts to Advance Gene-based Therapies for Ultra-Rare Neurological and Neuromuscular Disorders (U01 - Clinical Trial Optional)
Who won it before
5 competing awards (new and renewals) from FY2014 to FY2025 under this notice and the notices it replaced: $8,508,908 in first-year total cost, median $800,485.
Most frequent study sections
- Special Emphasis Panel[ZNS1 SRB-M (12)]3
- Special Emphasis Panel[ZNS1 SRB-M (15)]1
- Special Emphasis Panel[ZNS1 SRB-M (18)]1
Most frequent institutions
- BROAD INSTITUTE, INC.1
- COLUMBIA UNIVERSITY HEALTH SCIENCES1
- RESEARCH INST NATIONWIDE CHILDREN'S HOSP1
- UNIVERSITY OF PENNSYLVANIA1
- UT SOUTHWESTERN MEDICAL CENTER1
| FY | Project | PIs | Institution | First-year cost | Study section |
|---|---|---|---|---|---|
| 2024 | Silence ALS: A Platform for the Discovery and Development of Antisense Therapeutics for Patients with Ultra-Rare Forms of ALS1U01NS134684-01 · under PAR-22-030 | SHNEIDER, NEIL ALAN | COLUMBIA UNIVERSITY HEALTH SCIENCES, NY | $5,159,965 | ZNS1 |
| 2024 | IND-enabling studies of non-immunogenic gene therapy for ultra-rare DMD patients excluded from dystrophin trials1U01NS134672-01A1 · under PAR-22-030 | STEDMAN, HANSELL H | UNIVERSITY OF PENNSYLVANIA, PA | $1,541,019 | ZNS1 |
| 2023 | Advancement of Prion Protein-Lowering Divalent siRNA Therapy for Prion Disease1U01NS132994-01 · under PAR-22-030 | MINIKEL, ERIC VALLABH | BROAD INSTITUTE, INC., MA | $800,485 | ZNS1 |
| 2023 | IND-enabling studies for Aspartylglucosaminuria (AGU) to support the initiation of an AAV9/AGA gene transfer clinical trial1U01NS129339-01A1 · under PAR-22-030 | GRAY, STEVEN JIANNACCONE, SUSAN T | UT SOUTHWESTERN MEDICAL CENTER, TX | $631,697 | ZNS1 |
| 2023 | Viral Gene Therapy for Menkes Disease1U01NS129343-01A1 · under PAR-22-030 | KALER, STEPHEN GERARD | RESEARCH INST NATIONWIDE CHILDREN'S HOSP, OH | $375,742 | ZNS1 |
Data: Grants.gov's daily extract and NIH's notice pages and award files, in ScienceGraph release conductgrants-2026-11-09-0.1.0. An award is listed only where NIH's own record names the notice, and a PI only by NIH's profile ID. Grants.gov and NIH do not endorse ScienceDex.